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Transforming Lives Through New Treatments for Pompe Disease | #pompe Disease # Pompe Disease Market # Pompe Disease Forecast # Pompe Disease Companies # Pompe Disease Therapies # Pompe Disease Epidemiology # Pompe Disease Pipeline # Pompe Disease Market Size # Pompe Disease Market Trends

Transforming Lives Through New Treatments for Pompe Disease

Transforming Lives Through New Treatments for Pompe Disease

Pompe disease is a rare, progressive, and often life-threatening genetic disorder caused by mutations in the GAA (acid alpha-glucosidase) gene, leading to glycogen accumulation in muscle tissues. Over the years, significant advancements have been made in the treatment landscape, moving bey
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